Status | Study |
Recruiting |
Study Name: Biomarker for Maroteaux-Lamy Disease Condition: Maroteaux-lamy Disease Lysosomal Storage Diseases Date: 2011-10-24 |
Recruiting |
Study Name: Longitudinal Studies of Brain Structure and Function in MPS Disorders Condition: Mucopolysaccharidosis Type I Mucopolysaccharidosis Type II Date: 2011-08-02 |
Completed |
Study Name: Observational Study of Patients With Mucopolysaccharidosis (MPS) VI Who Previously Participated in ASB-00-02 Condition: MPS VI Date: 2011-06-29 |
Active, not recruiting |
Study Name: Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders Condition: Mucopolysaccharidosis Hurler Syndrome Hunter Syndrome Date: 2010-01-05 Interventions: Drug: Campath-1H Administered |
Terminated |
Study Name: Clinical Trial of Growth Hormone in MPS I, II, and VI Condition: Mucopolysaccharidosis I Mucopolysaccharidosis II Date: 2008-09-08 Interventions: Drug: Somatropin (DNA origin) The study starting dose of Nutropin AQ® will be 0.48 mg/kg/week divid |
Terminated |
Study Name: Hematopoietic Stem Cell Transplantation (HCT) for Inborn Errors of Metabolism Condition: Hurler's Syndrome Maroteaux-Lamy Syndrome Date: 2008-04-25 Interventions: Procedure: Stem Cell Transplantation |
Terminated |
Study Name: ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic Diseases Condition: Inherited Metabolic Diseases Lysosomal Storage Disorders P Date: 2008-04-03 Interventions: Biological: ALD-101 A subpopulation of cord blood cells composed of cells that express a high level of t |
Completed |
Study Name: A Phase 4 Two Dose Level Study of Naglazyme(TM) (Galsulfase) in Infants With MPS VI Condition: Mucopolysaccharidosis VI Maroteaux-Lamy S Date: 2006-03-02 Interventions: Drug: Naglazyme Weekly infusion for minimum of 52 weeks. Naglazyme is diluted in sterile 0.9% sodium chl |
Recruiting |
Study Name: Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP) Condition: Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Date: 2005-09-13 |
Completed |
Study Name: Stem Cell Transplantation for Hurler Condition: Mucopolysaccharidosis I Mucopolysaccharidosis VI Date: 2005-09-12 Interventions: Procedure: Stem Cell Transplant |